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amyloidosis clinical trials

FDA Drug Approval Process

August 24, 2022

Drugs are the lifeblood of patient treatments, and the development of new drugs is critical. Overseen by the FDA (U.S. Food and Drug Administration), in this blog we outline the phases and 12 steps required to develop and approve drugs.

Filed Under: Featured News, What Is Amyloidosis Tagged With: amyloidosis, amyloidosis clinical trials, amyloidosis research, amyloidosis research consortium, Boston medical center, clinical trials, FDA drug approval, mayo clinic, my amyloidosis pathfinder, what is a clinical trial

CRISPR/Cas9 – Editing the Code of Life

March 20, 2021

The scientific world is abuzz … a Nobel Prize-winning technology called CRISPR/Cas9 can now edit our DNA. This programmable gene-editing technology, which is efficient, precise, and scalable, has inspired a gold rush of countless applications in medicine, agriculture and basic science.  In this blog we invite you to read more about this ground-breaking advance and how, with one course of treatment, it could potentially cure hereditary transthyretin (hATTR / ATTRv) amyloidosis.

Filed Under: Featured News, What Is Amyloidosis Tagged With: #clinicaltrials, #crispr, #crispr/cas9, amyloidosis, amyloidosis clinical trials, amyloidosis news, amyloidosis treatment, ATTR amyloidosis, attrv, hATTR, Hereditary Amyloidosis, hereditaryamyloidosis

1st FDA-Approved Drug for AL Amyloidosis

January 16, 2021

After decades of relying on treatments approved for other diseases, on January 15, 2021 the FDA approved the first drug for AL Amyloidosis. Truly a game-changing, monumental advancement in the treatment of this disease.

Filed Under: Featured News, What Is Amyloidosis Tagged With: #Andromeda, AL amyloidosis, amyloidosis, amyloidosis clinical trials, amyloidosis news, amyloidosis treatment

Amyloidosis By The Numbers

August 23, 2019

An inside look into the state of amyloidosis today, based on 575 online responses. Read about patient demographics, symptoms, getting to a diagnosis through the physician community, treatments, and how life has changed post-treatment.

Filed Under: Featured News, What Is Amyloidosis Tagged With: amyloid assassin, amyloidosis, amyloidosis clinical trials, amyloidosis diagnosis, amyloidosis news, amyloidosis recovery, amyloidosis research, amyloidosis treatment, asct, bone marrow transplant, clinical trials, diagnosing amyloidosis, sct, stem cell transplant

Clinical Trials 101

October 17, 2018

Clinical research is simply medical research involving people. There are two types, clinical studies (aka observational studies) and clinical trials. In this blog, we explore clinical trials and the basics of what you need to know.

Filed Under: Featured News, What Is Amyloidosis Tagged With: amyloidosis, amyloidosis clinical trials, amyloidosis research, amyloidosis research consortium, Boston medical center, clinical trials, mayo clinic, my amyloidosis pathfinder, what is a clinical trial

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Recent News

  • FACES of Amyloidosis 2023
  • Hereditary Amyloidosis: The T60A Variant
  • Worldwide Hotspots of Hereditary ATTR Amyloidosis (ATTRv)
  • 2022: Mackenzie’s Mission – Our Report Card
  • CRISPR/Cas9 – ATTR Clinical Trial Update

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