“Mackenzie was so young that Dr. Gertz was “hard-pressed to believe she actually had the disease,” he tells us.
Around the world, activities are going on all month, culminating today, to raise awareness of the 7,000 rare diseases. Amyloidosis is one of those rare diseases. Together, great efforts are being made to take rare disease research to an international level. Only by doing so can we guarantee rare disease research will be truly effective. […]